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Gene editing advance shows promise as long-lasting treatment for rare liver disease
September 11, 2026
Medical ResearchMedical Xpress
Researchers have taken an important step toward solving one of the biggest challenges in gene therapy for children with metabolic liver disorders: growth itself. As a childs liver grows, some gene therapies that once worked can gradually lose their effect because the treated cells are eventually out
Researchers have taken an important step toward solving one of the biggest challenges in gene therapy for children with metabolic liver disorders: growth itself. As a childs liver grows, some gene therapies that once worked can gradually lose their effect because the treated cells are eventually outnumbered by new, untreated ones.
Source: Medical Xpress